Leaders with CureDuchenne say approvals are expected this year for several new treatments for Duchenne MD, making it "an ...

This retrospective review compared appendicular lean mass (ALM) and ALM index among patients with Duchenne muscular dystrophy (DMD) or Becker muscular dystrophy (BMD). Appendicular lean mass (ALM) and ...

DMD is the result of mutations in the dystrophin gene located on the X chromosome. These mutations lead to the absence or dysfunction of the dystrophin protein, which is essential for muscle stability ...

WORCESTER (CBS) -- Caring for a child with Duchenne Muscular Dystrophy can be incredibly challenging, but thanks to a local family's philanthropy and a local medical school's commitment, treatment is ...

Migvis Monduy, MD, medical director of Neuromuscular and Movement Disorders Programs at Nicklaus Children's Hospital, discussed challenges in Duchenne muscular dystrophy (DMD) treatment access and how ...

Using a new gene-editing technique, a team of scientists from UT Southwestern Medical Center stopped progression of Duchenne muscular dystrophy (DMD) in young mice. If efficiently and safely scaled up ...

There is no cure for DMD, but treatments can slow the progression of the disease and help improve quality of life. Duchenne muscular dystrophy (DMD) is a chronic condition that causes a gradual loss ...

The FDA has imposed a clinical hold on a Phase Ib trial assessing Pfizer’s mini-dystrophin gene therapy candidate PF-06939926 in Duchenne muscular dystrophy (DMD), after the company acknowledged the ...

Duchenne muscular dystrophy (DMD) causes muscle weakness that becomes more severe over time. While there is no cure, treatments can help slow the progression and manage symptoms and complications.