Cell membranes play a critical role by serving as containment units and separating the inner cellular space from the extracellular environment. Proteins with distinct functional units play a key role ...

Ikoma, Japan – Cell membranes play a critical role by serving as containment units and separating the inner cellular space from the extracellular environment. Proteins with distinct functional units ...

The Wiskott-Aldrich syndrome protein (WASp) is expressed exclusively in hematopoietic cells and presents either an autoinhibited or activated conformation. EG-011 is a first-in-class activator of the ...

A genetic disorder that leads to bleeding episodes and life-threatening infections has a new FDA approved treatment, a regulatory decision that marks two notable firsts — the first gene therapy for ...

Wiskott-Aldrich syndrome is a very rare genetic disorder that affects the WAS gene. Usually seen in males, it’s present from birth and characterized by a specific triad of symptoms. Wiskott-Aldrich ...